Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can alleviate symptoms. In the search for better treatment options, ...

The recent availability of 3 FDA-approved treatments for patients with spinal muscular atrophy (SMA) has dramatically altered patient outcomes and provided a wealth of new avenues for SMA research. A ...

The risk of scoliosis was largely related to what type of SMA a patient had, with those with type III having the lowest risk and those with type II developing scoliosis at a later age than those with ...

Spinal muscular atrophy (SMA) is a severe neurological disease for which there is presently no cure, although current therapies can alleviate symptoms. In the search for better treatment options, ...

SOUTH SAN FRANCISCO, Calif.--(BUSINESS WIRE)--Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), announced today that the U.S. Food and Drug Administration (FDA) has approved a New ...

On February 29, a groundbreaking original musical, Most Likely Not To…, is set to take place for one-night-only to amplify spinal muscular atrophy (SMA), a rare, progressive neuromuscular disease. One ...

Scholar Rock contends its experimental drug for spinal muscular atrophy can achieve what none of the currently available therapies can do to treat this rare disease. After positive data from a pivotal ...

Former Little Mix singer Jesy Nelson has opened up about her twin baby daughters being diagnosed with a rare genetic disorder that could mean they "probably will never walk." Jesy and her musician ...

Girlband star Jesy Nelson revealed in an emotional Instagram video that both of her twins had been diagnosed with a genetic condition called Spinal Muscular Atrophy (SMA), type 1. U.K.-based Nelson, ...